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Jyoti Sharma
Jyoti Sharma
Genzyme
Genetics
Diabetes mellitus
Biology
Internal medicine
Tolerability
4
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18
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Safety, tolerability and pharmacokinetics of oral venglustat in Parkinson disease patients with a GBA mutation
2019
Molecular Genetics and Metabolism
M. Judith Peterschmitt
Thomas Gasser
Stuart Isaacson
Jaime Kulisevsky
Pablo Mir
Tanya Simuni
Anne Marie Wills
Leonor Correia Guedes
Per Svenningsson
Cheryl Waters
Allena J. Ji
Jian Li
Pascal Minini
Blandine Nembo
Stéphane Saubadu
Jyoti Sharma
Tanya Fischer
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Citations (14)
Venglustat in adult Gaucher disease type 3: Preliminary safety, pharmacology, and exploratory efficacy from a phase 2 trial in combination with imiglucerase (LEAP)
2019
Molecular Genetics and Metabolism
Raphael Schiffmann
Eugen Mengel
Nigel Crawford
Sebastiaan J.M. Gaemers
Derralynn Hughes
Ana Jovanovic
Pascal Minini
Jyoti Sharma
Tanya Fischer
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Citations (3)
Evaluation of Glucosylceramide Synthase (GCS) Inhibition for GBA-Associated Parkinson’s Disease (P3.051)
2018
Neurology
Tanya Fischer
S. Pablo Sardi
Lamya S. Shihabuddin
Dan Rudin
Jyoti Sharma
Roberto Araujo
Jian Li
M. Judith Peterschmitt
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Citations (1)
Evaluation of glucosyl ceramide synthase (GCS) inhibition for GBA-associated Parkinson disease
2018
Molecular Genetics and Metabolism
M. Judith Peterschmitt
S. Pablo Sardi
Lamya S. Shihabuddin
Dan Rudin
Jyoti Sharma
Roberto Araujo
Jian Li
Tanya Fischer
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