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Andrea Shejtman
Andrea Shejtman
University College London
Immunology
Chronic granulomatous disease
Genetic enhancement
Medicine
p47 phox
3
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Gene Therapy with pCCLchimP47-phox Lentiviral Vector Achieves Long-term Reconstitution of NADPH Oxidase Activity in p47-phox Chronic Granulomatous Disease (CGD) Mouse Model
2018
The Journal of Allergy and Clinical Immunology
Walmir Cutrim Aragão Filho
Andrea Shejtman
Marta Zinicola
Ulrich Siler
Janine Reichenbach
Gaspar Bobby
Adrian J. Thrasher
Giorgia Santilli
Antonio Condino Neto
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Lentiviral Gene Therapy for p47(phox) Deficient Chronic Granulomatous Disease
2017
Andrea Shejtman
WC Aragao Filho
M. Weisser
M. Zinicola
Claire Booth
Siobhan O. Burns
Ulrich Siler
Janine Reichenbach
Hubert B. Gaspar
Antonio Condino Neto
Adrian J. Thrasher
Giorgia Santilli
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Development of a pCCLChim Lentiviral Vector for Gene Therapy of Patients with Chronic Granulomatous Disease (CGD) due to p47-phox Deficiency
2017
The Journal of Allergy and Clinical Immunology
Walmir Cutrim Aragão Filho
Andrea Shejtman
Marta Zinicola
Ulrich Siler
Janine Reichenbach
Hb Gaspar
Adrian J. Thrasher
Giorgia Santilli
Antonio Condino Neto
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