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Matthew Piechnik
Matthew Piechnik
Alfred I. duPont Hospital for Children
Molecular biology
Biology
Mucopolysaccharidosis
Dysplasia
Enzyme replacement therapy
3
Papers
42
Citations
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Mucopolysaccharidosis IVA: Diagnosis, Treatment, and Management
2020
International Journal of Molecular Sciences
Kazuki Sawamoto
José Víctor Álvarez González
Matthew Piechnik
Francisco Javier Sanjiao Otero
María L. Couce
Yasuyuki Suzuki
Shunji Tomatsu
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Citations (16)
Evading the AAV Immune Response in Mucopolysaccharidoses.
2020
International Journal of Molecular Sciences
Matthew Piechnik
Kazuki Sawamoto
Hidenori Ohnishi
Norio Kawamoto
Yasuhiko Ago
Shunji Tomatsu
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Citations (2)
Effect of enzyme replacement therapy on the growth of patients with Morquio A
2019
Journal of Human Genetics
Caitlin Doherty
Molly Stapleton
Matthew Piechnik
Robert W. Mason
William G. Mackenzie
Seiji Yamaguchi
Hironori Kobayashi
Yasuyuki Suzuki
Shunji Tomatsu
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Citations (24)
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