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L. van der Giessen
L. van der Giessen
Erasmus University Rotterdam
Alglucosidase alfa
Glycogen storage disease type II
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Gastroenterology
Diabetes mellitus
2
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5
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0
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Distal muscle weakness is a common and early feature in long-term enzyme-treated classic infantile Pompe patients.
2020
Orphanet Journal of Rare Diseases
J. van den Dorpel
Esther Poelman
L. Harlaar
H. A. van Kooten
L. van der Giessen
P.A. van Doorn
A.T. van der Ploeg
J. M. P. van den Hout
N.A.M.E. van der Beek
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Citations (2)
Effects of higher and more frequent dosing of alglucosidase alfa and immunomodulation on long-term clinical outcome of classic infantile Pompe patients.
2020
Journal of Inherited Metabolic Disease
Esther Poelman
Jja van den Dorpel
Marianne Hoogeveen-Westerveld
Jmp van den Hout
L. van der Giessen
Name van der Beek
W. Pijnappel
A.T. van der Ploeg
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Citations (3)
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