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Paula Overn
Paula Overn
Genetics
Genome editing
Biology
Diabetes mellitus
Bioinformatics
2
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Liver-targeting gene editing achieves significant neurological benefits in MPS I mice
2020
Molecular Genetics and Metabolism
Li Ou
Michael J. Przybilla
Ozan Ahlat
Paula Overn
Gerard O'Sullivan
Sarah Kim
Jeanine Jarnes
Chester B. Whitley
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Correction of both Tay-Sachs and Sandhoff diseases with the PS gene editing system
2020
Molecular Genetics and Metabolism
Li Ou
Michael J. Przybilla
Alexandru Flaviu Tăbăran
Paula Overn
Gerard O'Sullivan
Xuntian Jiang
Rohini Sidhu
Pamela Kell
Daniel S. Ory
Chester B. Whitley
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