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Prabhpreet S Bassi
Prabhpreet S Bassi
Biology
CRISPR
Cancer research
Genetics
Bioinformatics
4
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54
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NEW THERAPEUTIC APPROACHES AND THEIR READOUT
2018
Neuromuscular Disorders
Dwi U. Kemaladewi
Prabhpreet S Bassi
K Lindsay
S. Erwood
E. Hyatt
Kara M Place
R. Marks
Kinga I. Gawlik
Madeleine Durbeej
Evgueni A. Ivakine
Ronald D. Cohn
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A mutation-independent approach via transcriptional upregulation of a disease modifier gene rescues muscular dystrophy in vivo.
2018
bioRxiv
Dwi U. Kemaladewi
Prabhpreet S Bassi
Kyle Lindsay
Steven Erwood
Elzbieta Hyatt
Kara M Place
Ryan Marks
Kinga I. Gawlik
Madeleine Durbeej
Evgueni A. Ivakine
Ronald D. Cohn
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Citations (2)
Assessing the Therapeutic Potential of CRISPR/Cas9-Mediated Gene Modulation in Merosin-Deficient Congenital Muscular Dystrophy Type 1A
2017
Prabhpreet S Bassi
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Correction of a splicing defect in a mouse model of congenital muscular dystrophy type 1A using a homology-directed-repair-independent mechanism
2017
Nature Medicine
Dwi U. Kemaladewi
Eleonora Maino
Elzbieta Hyatt
Huayun Hou
Maylynn Ding
Kara M Place
Xinyi Zhu
Prabhpreet S Bassi
Zahra Baghestani
Amit G. Deshwar
Daniele Merico
Hui Yuan Xiong
Brendan J. Frey
Michael D. Wilson
Evgueni A. Ivakine
Ronald D. Cohn
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