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Gina Scarglia
Gina Scarglia
Glycosaminoglycan
Haematopoiesis
lentiviral transduction
Iduronate-2-sulfatase
Enzyme assay
2
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Ex vivo lentiviral transduction of hematopoietic stem cells in mucopolysaccharidosis type II (MPS II) mice achieves high levels of systemic iduronate-2-sulfatase (IDS) enzyme activity and normalization of glycosaminoglycans (GAGs)
2021
Molecular Genetics and Metabolism
Miles Smith
Lalitha R. Belur
Olivia Erlanson
Kelly M. Podetz-Pedersen
Andrea D. Karlen
Jessica McKenzie
Jenn Detellis
Khatuna Gagnidze
Geoff Parsons
Nicholas A. Robinson
Shelby LaBarre
Gina Scarglia
Saumil Shah
Hsing Chen Tsai
R. Scott McIvor
Melissa Bonner
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Shared inflammatory and skin-specific gene signatures reveal common drivers of discoid lupus erythematosus in canines, humans and mice
2021
Colton J. Garelli
Neil B. Wong
Cesar Piedra-Mora
Linda M. Wrijil
Gina Scarglia
Clément N. David
Ramón M. Almela
Nicholas A. Robinson
Jillian M. Richmond
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