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100. A multicentre retrospective survey of miglustat in patients with Niemann-Pick type C disease
100. A multicentre retrospective survey of miglustat in patients with Niemann-Pick type C disease
2009
Marc C. Patterson
Merci Pineda
Fridiric Sedel
Eugen Mengel
Wuh-Liang Hwu
Marianne Rohrbach
Brubo Bembi
Christoph Korenke
C. Luzy
Peter Schieber
Ruben Giorgino
Ed Wraith
Keywords:
Genetics
Miglustat
Pediatrics
Diabetes mellitus
Niemann-pick type c disease
Biology
in patient
retrospective survey
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