metabolic defects deaminase (ADA)-deficient mice and corrects their immune and Ex vivo gene therapy with lentiviral vectors rescues adenosine

doi:10.1182/blood-2006-05-023507Prepublished online July 11, 2006;2006 108: 2979-2988€€€€Antonia Follenzi, Luigi Naldini, Claudio Bordignon, Maria Grazia Roncarolo and Alessandro AiutiTabucchi, Maurilio Ponzoni, Francesca Sanvito, Claudio Doglioni, Clelia Di Serio, Luca Biasco, Alessandra Mortellaro, Raisa Jofra Hernandez, Matteo M. Guerrini, Filippo Carlucci, Antonella€